Sarepta DMD

Patients and Caregivers

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Overview of
Duchenne Treatments

Learn about treatment approaches for Duchenne muscular dystrophy (DMD) and explore options that may be right for you.

Exon skipping
Gene therapy
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Exon-Skipping Therapies

Exon-skipping therapy involves skipping over a certain exon (or section of a gene), depending on a person's genetic mutation. If a person is amenable, "skipping over" that exon can help the body to produce a shorter form of dystrophin.

Discover the possibilities of different exon-skipping therapies.

Exon 51 skipping therapy
Exon 53 skipping therapy
Exon 45 skipping therapy
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Support, by Your Side

SareptAssist is a support program available in the U.S. that pertains to Sarepta-approved therapies. It guides amenable patients and their families through the treatment journey and educates those who want to learn more before making a decision.

Sarepta Assist

Get Started

Call 1-888-SAREPTA (1-888-727-3782)

We’re available Monday through Friday, 8:30am – 6:30pm ET.

Spanish-speaking Case Managers and interpreters of other languages are available.

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